most citedA Two-Stage Patient-Focused Study Design for Rare Disease Controlled Trials

1 citations · 1 across the 1 of their papers we have counts for

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1 paper

stat.AP2016★ 1 cited

A Two-Stage Patient-Focused Study Design for Rare Disease Controlled Trials

Jian Yong, Sohaib H. Mohammad, Yan Yuan

We developed a study design for rare disease clinical trials (RDTs) that efficiently evaluate treatments, promotes access to new treatments during treatment development, and optimi…